Why is an AGU natural history study important?

The purpose of a Natural History Study of Aspartylglucosaminuria (AGU) is to better understand AGU. It aims to:

  • Understand and document the medical history, clinical characteristics, progression of symptoms, and medical events in individuals with AGU.
  • Provide greater understanding of AGU by determining outcome measures or a desired solution that a potential therapy could provide for use in future clinical trials.